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Table 5 Assumptions and variations for sensitivities

From: Establishing a reasonable price for an orphan drug

Sensitivity

− 20%

Base case

+ 20%

Non-orphan population sizea

80

100

120

Competition in non-orphan marketsb

40%

50%

60%

Market exclusivity of orphans

8 years

10 years

12 years

  1. aValues standardised per 50,000 inhabitants
  2. bValues of market share