From: Cost effectiveness of nusinersen for patients with infantile-onset spinal muscular atrophy in US
Utility value (BSC arm)
Source
Utility value (nusinersen arm)
Permanent ventilation
0.19
Thomson et al., 2017 [18]
Not sitting
0.29
Assumption
Sitting
0.60
Tappenden et al., 2018 [19]
0.65