From: Cost effectiveness of nusinersen for patients with infantile-onset spinal muscular atrophy in US
Baseline n = 81 | Day 64 n = 70 | Day 183 n = 65 | Day 302 n = 51 | Day 394 n = 48 | Day 578 n = 31 | Day 698 n = 17 | |
---|---|---|---|---|---|---|---|
% Achieving independent sitting (but not walking) | 0 | 1 | 5 | 10 | 15 | 29 | 24 |
% Achieving walking | 0 | 0 | 0 | 0 | 0 | 0 | 0 |