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Table 1 Motor function milestones achieved on nusinersen

From: Cost effectiveness of nusinersen for patients with infantile-onset spinal muscular atrophy in US

 

Baseline

n = 81

Day 64

n = 70

Day 183

n = 65

Day 302

n = 51

Day 394

n = 48

Day 578

n = 31

Day 698

n = 17

% Achieving independent sitting (but not walking)

0

1

5

10

15

29

24

% Achieving walking

0

0

0

0

0

0

0