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Table 3 Non-orphan, orphan and ultra-orphan population sizes.

From: Establishing a reasonable price for an orphan drug

 

Standardised per 50,000

Absolute

Orphan cut-off population

25

26,932

Orphan mid-point population

12.5

13,462

Ultra-orphan cut-off population

1

1077

Non-orphan average

100

107,732